ba0007p144 | (1) | ICCBH2019
Alves Ines
, Francisco Telma
, Pinto Helena
, Sousa Sergio
, Connor Paul
, Amorim Miguel
, Ramos Diogo
, Azevedo Sofia
, Vandewalle Bjorn
Objectives: Burosumab is an anti-FGF23 fully human monoclonal antibody, recently approved for the treatment of X-linked hypophosphatemia (XLH), presenting a novel treatment approach compared to conventional therapy (CT), composed of oral phosphate and active vitamin D. The objective of this study is to perform a Multi-Criteria Decision Analysis (MCDA) to assess the value of burosumab for the treatment of paediatric patients with XLH in Portugal, in comparison to CT.<p clas...